At $2.125 Million, New Gene Therapy Is The Most Expensive Drug Ever

The federal Food and Drug Administration has approved a gene therapy for a rare childhood disorder that is now the most expensive drug on the market. It costs $2.125 million per patient.

But for those patients lucky enough to get it, it appears it can save their lives with a one-time treatment.

Three-year-old Donovan Weisgarber is one of those patients. When he was born he seemed perfectly healthy. But within weeks, it became clear something was terribly wrong.

“It was about when he was about one month old that when we started to notice some symptoms,” says his mother, Laura Weisgarber, 32, of Columbus, Ohio.

Donovan started getting really fussy, stopped squirming, and got weaker and weaker.

Donovan had spinal muscular atrophy (SMA), a rare disorder caused by a defective gene; the illness destroys the nerves…

Original published: 2019-05-24 15:52:44 Read the full New York City News here


Some local news is curated - Original might have been posted at a different date/ time! Click the source link for details.

Leave a Reply

This site uses Akismet to reduce spam. Learn how your comment data is processed.

Send this to a friend